Leadership in Gene Therapy Corporate Presentation March 2023 Charles, Huntington’s disease patient advocate Our mission is to deliver curative, one-time administered genomic medicines that transform the lives of patients. Reimagining the future through ingenuity and innovation. Ron, a clinical trial patient for etranacogene dezaparvovec LLEEAADEDRESRHSIPH IIPN IGNE NGEE NTHEE TRHAEPYRAPY MMAARRCCHH 22002233 || 22 our history of innovation A gene therapy pioneer with a 25-year history and deeply engrained cu ...