Amicus Therapeutics: A Compelling Investment In The Rare Disease Biotech Sector
FOLDAmicus Therapeutics(FOLD) Seeking Alpha·2024-08-16 10:28
NicoElNino/iStock via Getty ImagesAmicus Therapeutics, Inc. (NASDAQ:FOLD) focuses on rare and orphan diseases, particularly Fabry and Pompe. The company’s portfolio includes Galafold and Pombiliti. Notably, Galafold is an oral treatment that seems effective for Fabry by stabilizing the dysfunctional enzyme alpha-Gal A. FOLD’s Pombiliti is a combination therapy with Opfolda, indicated for Pompe disease. Pombiliti replaces and stabilizes deficient or dysfunctional GAA enzymes needed for glycogen breakdown ...